Advancing Gene Therapy: One Breakthrough at a Time

Since 2013, AveXis has had one focus: bringing change to those devastated by genetic diseases.

The AveXis culture embraces this mission. As a compassionate and dedicated team, we are enthusiastic about the science behind our work, breaking barriers, and finding answers to difficult questions. We are dedicated to the SMA community, knowing that families affected—the patients in particular—are at the center of our efforts.

While we may not live the SMA experience, we appreciate it. And promise to support those impacted in every way we can, every time we can.


At AveXis, we have built a team with exceptional depth of experience, unified by a common vision: to develop gene therapies with the potential to positively impact the lives of the patients and families devastated by rare and life-threatening neurological genetic diseases. Though we are proud of what we have achieved to date, we remain relentlessly focused on making that vision a reality.